研究165 - 508 招聘
一个多中心, Observational Study to Evaluate the Real-World Outcomes of Pegvaliase (BMN 165) in Subjects with Phenylketonuria in Germany
指示
苯丙酮酸尿(北大)
目标
In addition to the efficacy and safety profile of pegvaliase that has been established in clinical trials; there remains an important need to provide data to prescribers and the phenylketonuria (PKU) community on the real-world usage of pegvaliase, 以及相关的结果, to support clinical practice optimization and provide greater understanding of important clinical issues in PKU
临床实验的治疗
Pegvaliase (BMN 165)
状态
这项研究目前正在招募参与者
研究类型
第四阶段